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Efficacy and Safety of 1500 mg Voxelotor in a Phase 2a Study (GBT440-007) in Adolescents with Sickle Cell Disease

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Year: 2018
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2018-99-117510
Authors: Clark Brown, Carolyn Hoppe, Adlette Inati, Miguel R. Abboud, Winfred Wang, Robert Liem, Gerald Woods, Lewis L. Hsu, Victor R. Gordeuk, Connie Piccone, Richard A. Drachtman, Erica Fong, Sandra Dixon, Margaret Tonda, Carla Washington, Joshua Lehrer-Graiwer
Institutions: Children's Healthcare of Atlanta, UCSF Benioff Children's Hospital, Rafik Hariri University Hospital, American University of Beirut Medical Center, St. Jude Children's Research Hospital, Lurie Children's Hospital, Children's Mercy Hospital, University of Illinois Chicago, Rainbow Babies & Children's Hospital, Rutgers Cancer Institute, Global Blood Therapeutics (United States)
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2906922470
Cites:
Cited by: 4
Related to: 10
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