Work

Lentiglobin Gene Therapy for Patients with Transfusion-Dependent β-Thalassemia (TDT): Results from the Phase 3 Northstar-2 and Northstar-3 Studies

Year: 2018

Type: conference-abstract

Source: Blood

DOI: 10.1182/blood-2018-99-112667

Authors: Franco Locatelli, Mark C. Walters, Janet L. Kwiatkowski, John Porter, Martin G. Sauer, Isabelle Thuret, Suradej Hongeng, Andreas E. Kulozik, Ashutosh Lal, Adrian J. Thrasher, Evangelia Yannaki, Heidi Elliot, Ge Tao, Mohammed Asmal, Alexis A. Thompson

Institutions: Bambino Gesù Children's Hospital, UCSF Benioff Children's Hospital, Children's Hospital of Philadelphia, University of Pennsylvania, University College Hospital, Medizinische Hochschule Hannover, Hôpital de la Timone, Mahidol University, Ramathibodi Hospital, Heidelberg University, European Molecular Biology Laboratory, European Molecular Biology Laboratory, University College London, G. Papanikolaou General Hospital, Bluebird Bio (United States), Northwestern University, Lurie Children's Hospital

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2910906997

Cites:

Cited by: 13

Related to: 10