Work

Meaningful treatment outcomes for Sanfilippo syndrome: A study of caregiver preferences and prioritization

Year: 2019

Type: article

Study design: Observational Study

Source: Molecular Genetics and Metabolism

DOI: 10.1016/j.ymgme.2018.12.285

Authors: Cara O'Neill, Katherine Porter, Elise Drake, Holly L. Peay

Institution: RTI International

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2912215217

FWCI: 0.86

Cites:

Cited by: 7

Related to: 10