Highly Efficient Therapeutic Gene Editing of BCL11A enhancer in Human Hematopoietic Stem Cells from ß-Hemoglobinopathy Patients for Fetal Hemoglobin Induction
Year: 2018
Type: conference-abstract
Source: Blood
Authors: Jing Zeng, Daniel E. Bauer, Yuxuan Wu, Benjamin P Roscoe, Pengpeng Liu, Qiuming Yao, Cicera Lazzarrotto, M. Kendell Clement, Mitchel A. Cole, Kevin Luk, Cristina Baricordi, Erica B. Esrick, John P Manis, David Dorfma, David A. Williams, Alessandra Biffi, Carlo Brugnara, Luca Biasco, Christian Brendel, Luca Pinello, Shengdar Tsai, Scot A. Wolfe
Institutions: Boston Children's Hospital, Harvard University, Dana-Farber Cancer Institute, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, University of Massachusetts Chan Medical School, St. Jude Children's Research Hospital, Massachusetts General Hospital, Brigham and Women's Hospital, Harvard Stem Cell Institute
Language: English
Subfield: Molecular Biology
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W2914529365