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Analysis of the baseline characteristics of Fabry disease patients screened for the pegunigalsidase alfa phase III BALANCE study

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Year: 2019
Type: article
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2018.12.389
Authors: David Warnock, Wallace Eric, Raphael Schiffmann, Myrl Holida, Ozlem Goker-Alpan, Robert Hopkin, Pilar Giraldo, Nedd Khan, Bojan Vujkovac, William Wilcox, Ales Linhart, Camilla Tøndel, Bruce A. Barshop, Amel Karaa, Maria Judit Molnar, Patrick Deegan, Jerry Vockley, William Rhead, Virginia Kimonis, Raul Chertkoff, Nicola Longo
Institutions: University of Alabama at Birmingham, Baylor University Medical Center, University of Iowa, O&O Alpan (United States), Cincinnati Children's Hospital Medical Center, Infusion Associates, Splošna Bolnišnica Slovenj Gradec, Emory University, Charles University, Haukeland University Hospital, University of California San Diego, Massachusetts General Hospital, Semmelweis University, University of Cambridge, University of Pittsburgh, Medical College of Wisconsin, University of California, Irvine, Protalix BioTherapeutics (Israel)
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: green
OpenAlex ID: W2914798647
FWCI: 0.172
Cites:
Cited by: 2
Related to: 10
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