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Therapeutic AAV Gene Transfer to the Nervous System: A Clinical Reality

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Year: 2019
Type: review
Source: Neuron
DOI: 10.1016/j.neuron.2019.02.017
Authors: Eloise Hudry, Luk H. Vandenberghe
Institutions: Harvard University, Harvard NeuroDiscovery Center, Massachusetts General Hospital, Broad Institute, Massachusetts Eye and Ear Infirmary, Harvard Stem Cell Institute
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: Lonza Houston, Foundation Fighting Blindness, Research to Prevent Blindness, Patrick and Aimee Butler Family Foundation, National Institutes of Health, National Institute on Aging
Awards: Role of apolipoprotein E in age and amyloid beta related neuronal dysfunction, APOE and neuroinflammation as modulators of glia-neuron communication via extracellular vesicles: implications for Alzheimer's disease, G760982372, Massachusetts Alzheimer's Disease Research Center (MADRC)
OpenAlex ID: W2921986557
FWCI: 6.039
Cites: 247
Cited by: 386
Related to: 10
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