Work

Open-Label Phase 2 Clinical Trial of ManNAc for GNE Myopathy (S23.008)

Year: 2019

Type: article

Source: Neurology

DOI: 10.1212/wnl.92.15_supplement.s23.008

Authors: Nuria Carrillo, Marjan Huizing, Petcharat Leoyklang, Melanie Quintana, Joseph Shrader, Kennan Bradley, Christina Slota, John Perreault, Bradley Class, Carla Ciccone, Rebecca Parks, Galen Joe, John Heiss, Scott Berry, May Christine Malicdan, William Gahl

Institutions: National Human Genome Research Institute, Berry Consultants, LLC (United States), RTI Health Solutions, National Institutes of Health, Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institute of Neurological Disorders and Stroke

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2966237196

FWCI: 0.286

Cites:

Cited by: 2

Related to: 10