Work

P.150Consistency of 48-week changes in North Star Ambulatory Assessment (NSAA) between Duchenne muscular dystrophy natural history data and clinical trial placebo arms, after adjustment for prognostic factors

Year: 2019

Type: article

Source: Neuromuscular Disorders

DOI: 10.1016/j.nmd.2019.06.206

Authors: N. Goemans, B. Wong, F. Muntoni, C. McDonald, E. Mercuri, A. Mazur, J. Signorovitch, G. Sajeev, H. Wong, I. Hussain, M. Jenkins, S. Ward

Institutions: Universitair Ziekenhuis Leuven, UMass Memorial Medical Center, Great Ormond Street Hospital, University College London, Università Cattolica del Sacro Cuore, Muscular Dystrophy UK, Analysis Group (United States)

Language: English

Topic: Muscle Physiology and Disorders

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2977038877

FWCI:

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