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Preclinical Studies for Sickle Cell Disease Gene Therapy Using Bone Marrow CD34+ Cells Modified with a βAS3-Globin Lentiviral Vector

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Year: 2011
Type: article
Source: Blood
DOI: 10.1182/blood.v118.21.3119.3119
Authors: Fabrizia Urbinati, Zulema Romero Garcia, Sabine Geiger, Rafael Ruiz de Assin, Gabriela Kuftinec, Roger P. Hollis, Satiro N. De Oliveira, Jennifer Wherley, Aaron Cooper, Tim M. Townes, Gay M. Crooks, Elizabeth J Read, Mark C. Walters, Herbert J. Meiselman, Thomas D. Coates, Victor J. Marder, Donald B. Kohn
Institutions: University of California, Los Angeles, University of Alabama at Birmingham, University of California, San Francisco, Children's Hospital Los Angeles
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2980417133
FWCI:
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Related to: 10
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