250 AVXS-101 phase 3 study in spinal muscular atrophy type 1
Year: 2019
Type: article
Authors: John W Day, Claudia A Chiriboga, Thomas O Crawford, Basil T Darras, Richard S Finkel, Anne M Connolly, Susan T Iannaccone, Nancy L Kuntz, Loren DM Peña, Meredith Schultz, Perry B Shieh, Edward C Smith, Imran Kausar, Douglas E Feltner, Francis G Ogrinc, Haojun Ouyang, Thomas A Macek, Elaine Kernbauer, Lynlee M Muehring, James L’Italien, Douglas M Sproule, Brian K Kaspar, Jerry R Mendell
Institutions: Stanford Medicine, Stanford University, Columbia University Irving Medical Center, Johns Hopkins Medicine, Boston Children's Hospital, Nemours Children's Clinic, Nationwide Children's Hospital, The Ohio State University, The University of Texas Southwestern Medical Center, Lurie Children's Hospital, Cincinnati Children's Hospital Medical Center, University of Cincinnati, University of California, Los Angeles, Duke University, Duke Medical Center
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W2986287334