Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS
Year: 2019
Type: article
Source: Nature Medicine
Authors: Mariana Bravo-Hernandez, Takahiro Tadokoro, Michael R. Navarro, Oleksandr Platoshyn, Yoshiomi Kobayashi, Silvia Marsala, Atsushi Miyanohara, Stefan Juhas, Jana Juhasova, Helena Skalnikova, Zoltan Tomori, Ivo Vanicky, Hana Studenovska, Vladimir Proks, PeiXi Chen, Noe Govea-Perez, Dara Ditsworth, Joseph D. Ciacci, Shang Gao, Wenlian Zhu, Eric T. Ahrens, Shawn P. Driscoll, Thomas D. Glenn, Melissa McAlonis-Downes, Sandrine Da Cruz, Samuel L. Pfaff, Brian K. Kaspar, Don W. Cleveland, Martin Marsala
Institutions: University of California San Diego, University of the Ryukyus, Czech Academy of Sciences, Institute of Animal Physiology and Genetics, Slovak Academy of Sciences, Institute of Experimental Physics of the Slovak Academy of Sciences, Institute of Neurobiology of the Slovak Academy of Sciences, Czech Academy of Sciences, Czech Academy of Sciences, Institute of Macromolecular Chemistry, Ludwig Cancer Research, Ludwig Cancer Research, Salk Institute for Biological Studies, Howard Hughes Medical Institute
Language: Dutch
Subfield: Genetics
Domain: Life Sciences
Open Access status: green
OpenAlex ID: W2996712947
