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Pharmacological Inhibition of Nemo-like Kinase Rescues mTOR-Mediated Translation and Primes Progenitors for Leucine-Stimulated Erythroid Expansion in Pre-Clinical Models of Diamond Blackfan Anemia

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Year: 2019
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2019-129570
Authors: Mark C Wilkes, Jacqueline D Mercado, Mallika Saxena, Jun Chen, Kavitha Siva, Hee-Don Chae, Minyoung Youn, Ethan Patrick Wentworth, Kevin Jung, Ryan Sathianathen, Hiral Patel, Bertil Glader, Anupama Narla, Claire E Repellin, Hanna T Gazda, Manuel Serrano, Johan Flygare, Kathleen M. Sakamoto
Institutions: Stanford Medicine, Stanford University, Lund University, SRI International, Boston Children's Hospital, Manton Center for Orphan Disease Research, Institute for Research in Biomedicine
Language: English

Topic: Blood disorders and treatments
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2997702196
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Related to: 10
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