Work

AAV2-hCHM Subretinal Delivery to the Macula in Choroideremia: 2 year Results of an Ongoing Phase I/II Gene Therapy Trial

Year: 2019

Type: article

Source: Investigative Ophthalmology & Visual Science

Authors: Tomas S. Alemán, Rachel M. Huckfeldt, Leona Serrano, Grace K. Vergilio, Denise J. Pearson, Katherine E. Uyhazi, Sarah McCague, Kathleen Marshall, Daniel C. Chung, Emily Liu, Eric A. Pierce, Jessica Ijams Wolfing Morgan, Jean Bennett, Dean Eliott, Jason Comander, Albert M. Maguire

Institutions: University of Pennsylvania, Massachusetts Eye and Ear Infirmary, Harvard University, Children's Hospital of Philadelphia, Spark Therapeutics (United States)

Language: English

Topic: Retinal Development and Disorders

Subfield: Ophthalmology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: gold

Estimated APC paid: $1,850

OpenAlex ID: W3007202623

FWCI: 1.448

Cites:

Cited by: 6

Related to: 10