Work

Current and future gene therapies for hemoglobinopathies

Year: 2020

Type: article

Source: Current Opinion in Hematology

DOI: 10.1097/moh.0000000000000581

Authors: Christian Brendel, David A. Williams

Institutions: Boston Children's Hospital, Harvard University, Dana-Farber Cancer Institute

Language: English

Topic: Hemoglobinopathies and Related Disorders

Subfield: Genetics

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: Kenneth Rainin Foundation, National Heart, Lung, and Blood Institute

Awards: G3378280475, G3518503472, Gene therapy targeting BCL11A to induce fetal hemoglobin and reduce sickle hemoglobin in patients with Sickle Cell Disease

OpenAlex ID: W3012606264

FWCI: 1.311

Cites: 49

Cited by: 14

Related to: 10