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Phase 1 Clinical Trial of Losmapimod in Facioscapulohumeral Muscular Dystrophy (FSHD): Safety, Tolerability, and Target Engagement (1557)

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Year: 2020
Type: article
Source: Neurology
DOI: 10.1212/wnl.94.15_supplement.1557
Authors: Michelle Mellion, Lucienne Ronco, Lorin Thompson, Michelle Hage, Sander Brooks, Emilie van Brummelen, Lisa Pagan, Umesh Badrising, Shane Raines, William Tracewell, Baziel van Engelen, Geert-Jan Groeneveld, Diego Cadavid
Institutions: Fulcrum Therapeutics (United States), Centre for Human Drug Research, Leiden University Medical Center, Radboud University Medical Center
Language: English

Topic: Muscle Physiology and Disorders
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W3043311202
FWCI: 0.243
Cites:
Cited by: 3
Related to: 10
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