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Nusinersen in Infantile-onset Spinal Muscular Atrophy: Results from Longer-term Treatment from the Open-label SHINE Extension Study (1640)

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Year: 2020
Type: article
Source: Neurology
DOI: 10.1212/wnl.94.15_supplement.1640
Authors: Diana Castro, Richard S. Finkel, Michelle A. Farrar, Mar Tulinius, Kristin J. Krosschell, Kayoko Saito, Giulia Gambino, Richard Foster, Ishir Bhan, Janice Wong, Boris Kandinov, Wildon Farwell
Institutions: The University of Texas Southwestern Medical Center, Nemours Children's Health System, UNSW Sydney, Sydney Children's Hospital, University of Gothenburg, Northwestern University, Tokyo Women's Medical University, Biogen (United States)
Language: English

Topic: Neurogenetic and Muscular Disorders Research
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W3093330457
FWCI: 1.809
Cites:
Cited by: 23
Related to: 10
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