Resolution of Serious Vaso-Occlusive Pain Crises and Reduction in Patient-Reported Pain Intensity: Results from the Ongoing Phase 1/2 HGB-206 Group C Study of LentiGlobin for Sickle Cell Disease (bb1111) Gene Therapy
Year: 2020
Type: article
Study design: Clinical Trial
Source: Blood
Authors: Alexis A. Thompson, Mark C. Walters, Markus Y Mapara, Janet L. Kwiatkowski, Lakshmanan Krishnamurti, Banu Aygun, Kimberly A. Kasow, Stacey Rifkin-Zenenberg, Manfred Schmidt, Jay DelCarpini, Francis J. Pierciey, Alexandra L. Miller, Meghan E. Gallagher, Ren Chen, Sunita Goyal, Julie Kanter, John F. Tisdale
Institutions: Northwestern University, Lurie Children's Hospital, UCSF Benioff Children's Hospital, Columbia University Irving Medical Center, Children's Hospital of Philadelphia, University of Pennsylvania, Emory University, Children's Healthcare of Atlanta, Donald & Barbara Zucker School of Medicine at Hofstra/Northwell, Cohen Children's Medical Center, University of North Carolina at Chapel Hill, Hackensack University Medical Center, Bluebird Bio (United States), University of Alabama at Birmingham, National Institutes of Health, National Institute of Diabetes and Digestive and Kidney Diseases, National Heart, Lung, and Blood Institute
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W3095009176