Long-Term Efficacy and Safety of Betibeglogene Autotemcel Gene Therapy for the Treatment of Transfusion-Dependent β-Thalassemia: Results in Patients with up to 6 Years of Follow-up
Year: 2020
Type: article
Source: Blood
Institutions: Children's Hospital of Philadelphia, University of Pennsylvania, UCSF Benioff Children's Hospital, Mahidol University, Ramathibodi Hospital, Bambino Gesù Children's Hospital, The University of Sydney, Royal Prince Alfred Hospital, Centenary Institute, Hôpital Necker-Enfants Malades, Sorbonne Paris Cité, Assistance Publique – Hôpitaux de Paris, Hôpitaux Universitaires Paris-Ouest, Institut des Maladies Génétiques Imagine, Université Paris Descartes, Bluebird Bio (United States), Northwestern University, Lurie Children's Hospital
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W3095573674