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Improvements in Health-Related Quality of Life for Patients Treated with LentiGlobin for Sickle Cell Disease (bb1111) Gene Therapy

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Year: 2020
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2020-136193
Authors: Julie Kanter, John F. Tisdale, Markus Y Mapara, Janet L. Kwiatkowski, Lakshmanan Krishnamurti, Ren Chen, Meghan E. Gallagher, Yuchen Ding, Sunita Goyal, Clark Paramore, Alexis A. Thompson, Mark C. Walters
Institutions: University of Alabama at Birmingham, National Institutes of Health, National Institute of Diabetes and Digestive and Kidney Diseases, National Heart, Lung, and Blood Institute, Columbia University, Children's Hospital of Philadelphia, University of Pennsylvania, Emory University, Children's Healthcare of Atlanta, Bluebird Bio (United States), Northwestern University, Lurie Children's Hospital, UCSF Benioff Children's Hospital
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W3097296548
Cites:
Cited by: 8
Related to: 10
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