Work

Delivery technologies for in utero gene therapy

Year: 2020

Type: review

Source: Advanced Drug Delivery Reviews

DOI: 10.1016/j.addr.2020.11.002

Authors: Rohan Palanki, William H. Peranteau, Michael J. Mitchell

Institutions: University of Pennsylvania, Children's Hospital of Philadelphia, Abramson Cancer Center

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: American Cancer Society, Burroughs Wellcome Fund, Abramson Cancer Center, Canadian Aeronautics and Space Institute, National Institutes of Health, Harvard School of Engineering and Applied Sciences, National Heart, Lung, and Blood Institute, National Cancer Institute, National Institute of Diabetes and Digestive and Kidney Diseases, National Center for Advancing Translational Sciences

Awards: A data-driven drug delivery (4D) platform for probing and treating the chemoresistant bone marrow microenvironment, Prenatal pulmonary cell gene editing to cure monogenic lung diseases, G2294837937, G4164033398, In utero gene editing to cure a metabolic liver disease, Modular approach for the delivery of antibodies into the cytoplasm of cells, In utero CRISPR-mediated gene editing to cure congenital monogenic disorders, Targeting stem-like cells and their niche in pancreatic cancer, Abramson Cancer Center Support Grant

OpenAlex ID: W3098908552

FWCI: 0.827

Cites: 172

Cited by: 64

Related to: 10