Work

Elivaldogene Autotemcel (eli-cel, Lenti-D) Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy: Updated Results from the Phase 2/3 ALD-102 Study and First Report on Safety Outcomes from the Phase 3 ALD-104 Study

Year: 2021

Type: article

Source: Transplantation and Cellular Therapy

DOI: 10.1016/s2666-6367(21)00149-4

Authors: Paul J. Orchard, Christine N. Duncan, Florian S. Eichler, Satiro N. De Oliveira, Adrian J. Thrasher, Caroline Sevin, Hernan M. Amartino, Nicholas J.C. Smith, Jörn-Sven Kühl, Daniel Kenney-Jung, Robert Chiesa, Jean-Hugues Dalle, Jing Xu, Andrew C. Dietz, Elizabeth McNeil, Patrick Aubourg, David A. Williams

Institutions: Women's and Children's Hospital, Bluebird Bio (United States)

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: hybrid

Estimated APC paid: $3,650

OpenAlex ID: W3128466817

FWCI: 0.252

Cites:

Cited by: 2

Related to: 10