Work

Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models

Year: 2021

Type: article

Source: Neurotherapeutics

DOI: 10.1007/s13311-021-01040-7

Authors: Emrah Gumusgoz, Dikran R Guisso, Sahba Kasiri, Jun Wu, Matthew Dear, Brandy Verhalen, Silvia Nitschke, Sharmistha Mitra, Felix Nitschke, Berge A. Minassian

Institutions: The University of Texas Southwestern Medical Center, Corteva (United States)

Language: English

Topic: Glycogen Storage Diseases and Myoclonus

Subfield: Rheumatology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: bronze

Funders: Massachusetts Institute of Technology, Harvard University, National Institutes of Health, National Institute of Neurological Disorders and Stroke

Awards: G3718196111, G9000123538

OpenAlex ID: W3130326418

FWCI: 5.938

Cites: 60

Cited by: 50

Related to: 10