Maralixibat Treatment Significantly Reduces Pruritus and Serum Bile Acids in Patients with Alagille Syndrome: Results from a Randomized Phase II Study with 4 Years of Follow-Up
Year: 2020
Type: preprint
Study design: Clinical Trial
Source: SSRN Electronic Journal
DOI: 10.2139/ssrn.3756810
Authors: Emmanuel Gonzales, Winita Hardikar, Michael Stormon, Alastair Baker, Loreto Hierro, Dorota Gliwicz, Florence Lacaille, Alain Lachaux, Ekkehard Sturm, Kenneth Setchell, Ciara Kennedy, Alejandro Dorenbaum, Jana Steinmetz, Niraz Desai, Andrew James Wardle, Pamela Vig, Thomas Jaecklin, Etienne Sokal, Emmanuel Jacquemin
Institutions: Université Paris-Saclay, Assistance Publique – Hôpitaux de Paris, Bicêtre Hospital, Royal Children's Hospital, Children's Hospital at Westmead, King's College Hospital, Hospital Universitario La Paz, Children's Memorial Health Institute, Hôpital Necker-Enfants Malades, Hôpital Femme Mère Enfant, Cincinnati Children's Hospital Medical Center, University of Cincinnati, Amplyx Pharmaceuticals (United States), Stanford Medicine, Stanford University, Takeda (Japan), Cliniques Universitaires Saint-Luc, UCLouvain
Language: English
Subfield: Surgery
Field: Medicine
Domain: Health Sciences
Open Access status: green
OpenAlex ID: W3132052349