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The brain penetrant PPARγ agonist leriglitazone restores multiple altered pathways in models of X-linked adrenoleukodystrophy

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Year: 2021
Type: article
Source: Science Translational Medicine
DOI: 10.1126/scitranslmed.abc0555
Authors: Laura Rodríguez-Pascau, Anna Vilalta, Marc Cerrada, Estefania Traver, Sonja Forss-Petter, Isabelle Weinhofer, Jan Bauer, Stephan Kemp, Guillem Pina, Sílvia Pascual, Uwe Meya, Patricia L. Musolino, Johannes Berger, Marc Martinell, Pilar Pizcueta
Institutions: Medical University of Vienna, Amsterdam UMC Location University of Amsterdam, Amsterdam University Medical Centers, University of Amsterdam, Massachusetts General Hospital
Language: English

Topic: Metabolism and Genetic Disorders
Subfield: Clinical Biochemistry
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: Centro para el Desarrollo Tecnológico Industrial, Generalitat de Catalunya, Politechnika Poznańska, Horizon 2020 Framework Programme
Awards: G2510321663, G3567708089, G4801232681, G6183770678
OpenAlex ID: W3165292144
FWCI: 5.836
Cites: 69
Cited by: 42
Related to: 10
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