Work

AVXS-101 Gene-Replacement Therapy (GRT) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update (P1.6-057)

Year: 2019

Type: article

Source: Neurology

DOI: 10.1212/wnl.92.15_supplement.p1.6-057

Authors: Meredith Schultz, Kathryn Swoboda, Michelle Farrar, Hugh McMillan, Julie Parsons, Courtney Wells, Francis G. Ogrinc, Bryan McGill, Douglas E. Feltner, James L’Italien, Douglas M. Sproule, Kevin A. Strauss

Institutions: University of Wisconsin–Madison, Massachusetts General Hospital, Sydney Children's Hospital, Children's Hospital of Eastern Ontario, Children's Hospital Colorado, Clinic for Special Children

Language: English

Topic: Neurogenetic and Muscular Disorders Research

Subfield: Genetics

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W3187676111

FWCI: 0.137

Cites:

Cited by: 2

Related to: 10