Work

Rational engineering of a functional CpG-free ITR for AAV gene therapy

Year: 2021

Type: article

Source: Gene Therapy

DOI: 10.1038/s41434-021-00296-0

Authors: Xiufang Pan, Yongping Yue, Maria Boftsi, Lakmini P. Wasala, Ngoc Tam Tran, Keqing Zhang, David J. Pintel, Phillip W. L. Tai, Dongsheng Duan

Institutions: University of Missouri, University of Massachusetts Chan Medical School

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: National Institute of Allergy and Infectious Diseases, National Institute of Neurological Disorders and Stroke, National Institute of Arthritis and Musculoskeletal and Skin Diseases

Awards: G2537392460, Treatment of Duchenne Muscular Dystrophy with the Muscle Calcium Pump, G5179575593

OpenAlex ID: W3202703601

FWCI: 4.211

Cites: 92

Cited by: 53

Related to: 10