Work

Use of Elamipretide in Patients Assigned Treatment in the Compassionate Use Program: Case Series in Four Rare Orphan Diseases

Year: 2021

Type: preprint

Source: Research Square

DOI: 10.21203/rs.3.rs-927266/v1

Authors: Mary Kay Koenig, S. Nick Russo, Kim L. McBride, Hans Tomas Bjornsson, Brynja Bjork Gunnarsdottir, Amy Goldstein, Scott A. Falk

Institutions: The University of Texas Health Science Center at Houston, Nationwide Children's Hospital, National University Hospital of Iceland, Children's Hospital of Philadelphia, University of Pennsylvania

Language: English

Topic: Mitochondrial Function and Pathology

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: Children's Hospital of Philadelphia, University of Pennsylvania, Perelman School of Medicine, University of Pennsylvania

OpenAlex ID: W3206932041

Cites: 9

Cited by:

Related to: 10