Work

Delivery of therapeutic AAV9 vectors via cisterna magna to treat neurological disorders

Year: 2021

Type: article

Source: Trends in Molecular Medicine

DOI: 10.1016/j.molmed.2021.09.007

Authors: Paolo M. Marchi, Lara Marrone, Mimoun Azzouz

Institution: University of Sheffield

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

Funder: Medical Research Council

Awards: Gene Therapy Innovation and Manufacturing Centre (GTIMC), JPND - Multicellular organoids: modeling, mechanisms and therapy development for C9ORF72-associated neurodegeneration.

OpenAlex ID: W3210278627

FWCI: 1.492

Cites: 11

Cited by: 21

Related to: 10