Work

Escalating Dose and Randomized, Controlled Study of Nusinersen in Participants with Spinal Muscular Atrophy; Study Design of the Phase 2/3 DEVOTE (232SM203) Study to Explore High Dose Nusinersen (1169)

Year: 2020

Type: article

Study design: Study Protocol

Source: Neurology

DOI: 10.1212/wnl.94.15_supplement.1169

Authors: Richard S. Finkel, John W. Day, Nancy Mitchell-Sweeney, Richard Foster, Peng Sun, Ishir Bhan, Boris Kandinov, Wildon Farwell

Institutions: Nemours Children's Health System, Stanford Medicine, Stanford University, Biogen (United States)

Language: English

Topic: Neurogenetic and Muscular Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W3216841027

FWCI:

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Related to: 10