Betibeglogene Autotemcel Gene Therapy for Non–β 0 /β 0 Genotype β-Thalassemia
Work
Year: 2021
Type: article
Abstract: Betibeglogene autotemcel (beti-cel) gene therapy for transfusion-dependent β-thalassemia contains autologous CD34+ hematopoietic stem cells and progenitor cells transduced with the BB305 lentiviral ve... more
Source: New England Journal of Medicine
Authors Franco Locatelli, Alexis A. Thompson, Janet L. Kwiatkowski, John B. Porter, Adrian J. Thrasher +19 more
Institutions Bambino Gesù Children's Hospital, Istituti di Ricovero e Cura a Carattere Scientifico, Sapienza University of Rome, Lurie Children's Hospital, Children's Hospital of Philadelphia +13 more
Cites: 37
Cited by: 161
Related to: 10
FWCI: 25.86
Citation percentile (by year/subfield): 86.74
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Sustainable Development Goal Good health and well-being
Open Access status: bronze
Funder bluebird bio