eP195: Safety and efficacy of Copper Histidinate (CUTX-101) treatment for Menkes disease caused by severe loss-of-function variants in ATP7A
Year: 2022
Type: article
Source: Genetics in Medicine
Authors: Stephen Kaler, Shama Munim, Michael Chen, Robert Niecestro, Lung Yam
Institution: Nationwide Children's Hospital
Language: English
Topic: Trace Elements in Health
Subfield: Nutrition and Dietetics
Field: Nursing
Domain: Health Sciences
Open Access status: bronze
OpenAlex ID: W4220674523
