Comparison of Outcomes in Patients with Cerebral Adrenoleukodystrophy (CALD) Receiving Elivaldogene Autotemcel (eli-cel; Lenti-D) Gene Therapy in Clinical Trials Versus Those Receiving Allogeneic Hematopoietic Stem Cell Transplant in a Contemporaneous Comparator Study
Year: 2022
Type: article
Authors: Christine N. Duncan, Jörn-Sven Kühl, Robert Chiesa, Jaap-Jan Boelens, Florian Eichler, Caroline Sevin, Jean-Hugues Dalle, Satiro N. De Oliveira, Hernan M. Amartino, Neena Kapoor, Vinod K. Prasad, Simon Jones, Mattia Algeri, Nancy J. Bunin, Cristina Diaz-de-Heredia, Adrian J. Thrasher, Juliana Folloni Fernandes, Nicholas Smith, Ami J Shah, Franco Locatelli, Marc Engelen, Caroline A. Lindemans, Andrew C. Dietz, Lin Pan, Jakob Sieker, David A. Williams, Paul J. Orchard
Language: English
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
Open Access status: hybrid
Estimated APC paid: $3,650
OpenAlex ID: W4220891229