Work

A phase 1/2 open label extension study of givosiran, an investigational RNAi therapeutic, in patients with acute intermittent porphyria

Year: 2020

Type: article

Study design: Observational Study

Source: Journal of Hepatology

DOI: 10.1016/s0168-8278(20)31580-4

Authors: Penelope Stein, David Rees, Karl Anderson, Herbert Bonkovsky, Eliane Sardh, Pauline Harper, Manisha Balwani, Charles Parket, John Phillips, Daphne Vassiliou, Craig Penz, Amy Chan, Gary Liu, Amy Simon, D Montgomery Bissell

Language: English

Topic: Porphyrin Metabolism and Disorders

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: bronze

OpenAlex ID: W4238805665

FWCI: 0.65

Cites:

Cited by: 10

Related to: 10