Faculty Opinions recommendation of Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction.
Year: 2016
Type: peer-review
Author: Fabio Candotti
Institution: Centre Hospitalier Universitaire Vaudois
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4251336117
