Pharmacotherapy for Spinal Muscular Atrophy in Babies and Children: A Review of Approved and Experimental Therapies
Year: 2022
Type: review
Source: Pediatric Drugs
Author: Claudia A. Chiriboga
Institution: Columbia University Irving Medical Center
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4293872979
