638 Splice-switching antisense oligonucleotides for the treatment of class I cystic fibrosis transmembrane conductance regulator mutations
Year: 2022
Type: article
Source: Journal of Cystic Fibrosis
Institution: Rosalind Franklin University of Medicine and Science
Language: English
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
Open Access status: bronze
Funder: Cystic Fibrosis Foundation
OpenAlex ID: W4300863364
