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Base Editing for Therapeutic Induction of Fetal Hemoglobin in β-Thalassemia

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Year: 2022
Type: article
Source: Blood
DOI: 10.1182/blood-2022-169391
Authors: Georgios E. Christakopoulos, Thiyagaraj Mayuranathan, Alfonso G. Fernandez, Kalin Mayberry, Yu Yao, Rahul Telange, Michael Dudley, Rachel Levine, Erin Dempsey, David R. Liu, Jonathan S Yen, Mitchell J. Weiss
Institutions: St. Jude Children's Research Hospital, Broad Institute, Howard Hughes Medical Institute, Harvard University, Beam Therapeutics (United States)
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4310107095
FWCI: 0.155
Cites:
Cited by: 1
Related to: 10
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