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Effect of Luspatercept on Red Blood Cell (RBC) Transfusion Burden, Iron Chelation Therapy (ICT), and Iron Overload in Adults with Transfusion-Dependent β-Thalassemia (TDT) from the BELIEVE Trial: A Long-Term Analysis

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Year: 2022
Type: article
Source: Blood
DOI: 10.1182/blood-2022-156985
Authors: Olivier Hermine, Maria Domenica Domenica Cappellini, Ali T. Taher, Thomas D. Coates, Vip Viprakasit, Antonis Kattamis, Jeevan K. Shetty, Marija Bosilkovska Weisskopf, Natalia Holot, Sadanand Vodala, Wen-Ling Kuo, John B. Porter
Institutions: Hôpital Necker-Enfants Malades, Inserm, Université Paris Cité, Assistance Publique – Hôpitaux de Paris, Institut des Maladies Génétiques Imagine, University of Milan, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, American University of Beirut Medical Center, University of Southern California, Children's Hospital Los Angeles, Mahidol University, National and Kapodistrian University of Athens, Bristol-Myers Squibb (Switzerland), Bristol-Myers Squibb (United States), University College London
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4310114314
FWCI: 0.778
Cites:
Cited by: 7
Related to: 10
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