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Gene therapies for RyR1-related myopathies

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Year: 2022
Type: review
Source: Current Opinion in Pharmacology
DOI: 10.1016/j.coph.2022.102330
Authors: Isabelle Marty, Mathilde Beaufils, Julien Fauré, John Rendu
Institutions: Inserm, Grenoble Institute of Neurosciences, Université Grenoble Alpes
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: Association Française contre les Myopathies, Région Auvergne-Rhône-Alpes
OpenAlex ID: W4312095268
FWCI: 0.213
Cites: 34
Cited by: 7
Related to: 10
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