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A first-in-human phase 1 clinical gene therapy trial for the treatment of heart failure using a novel rationally designed cardiotropic adeno-associated vector

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Year: 2022
Type: article
Source: Journal of Molecular and Cellular Cardiology
DOI: 10.1016/j.yjmcc.2022.08.225
Authors: Monica Alvisi, Timothy Henry, Eugene Chung, Jay Traverse, Leigh Ervin, Shiva Krupa, Hesham Sadek, Canwen Jiang, Sheila Mikhail, Kobra Haghighi, Evangelia Kranias, Jude Samulski, Anna Tretalova, Roger Hajjar
Institutions: Christ Hospital, Minneapolis Heart Institute Foundation, AskBio (United States), The University of Texas Southwestern Medical Center, University of Cincinnati, Flagship Pioneering (United States)
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4313397361
FWCI: 0.27
Cites:
Cited by: 4
Related to: 10
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