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Psychometric properties of QI-Disability in CDKL5 Deficiency Disorder: Establishing readiness for clinical trials

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Year: 2023
Type: article
Study design: Observational Study
Source: Epilepsy & Behavior
DOI: 10.1016/j.yebeh.2022.109069
Authors: Jacinta M. Saldaris, Peter Jacoby, Helen Leonard, Tim A. Benke, Scott Demarest, Eric D. Marsh, Jenny Downs
Institutions: The Kids Research Institute Australia, The University of Western Australia, Children's Hospital Colorado, University of Colorado Anschutz, Children's Hospital of Philadelphia, University of Pennsylvania, Curtin University
Language: English

Topic: Epilepsy research and treatment
Subfield: Psychiatry and Mental health
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: HCA International Foundation, International Foundation for CDKL5 Research, National Institutes of Health, National Institute of Neurological Disorders and Stroke
Award: Multi-Site Validation of Biomarkers and Core Clinical Outcome Measures for Clinical Trials Readiness in CDKL5 Deficiency Disorder
OpenAlex ID: W4315928875
FWCI: 1.734
Cites: 31
Cited by: 9
Related to: 10
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