Work

Preclinical enzyme replacement therapy with a recombinant β-galactosidase-lectin fusion for CNS delivery and treatment of GM1-gangliosidosis

Year: 2023

Type: article

Study design: Observational Study

Source: Molecular Genetics and Metabolism

DOI: 10.1016/j.ymgme.2022.107356

Authors: Jason A. Weesner, Diantha van de Vlekkert, Walter L. Acosta, Tianhong Yang, Elida M. Gomero, Huimin Hu, David Radin, Carole L. Cramer, Alessandra d'Azzo

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4319456134

FWCI:

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