Work

Real-world impact of enzyme replacement therapy on endurance in patients with MPS IVA

Year: 2023

Type: article

Study design: Observational Study

Source: Molecular Genetics and Metabolism

DOI: 10.1016/j.ymgme.2022.107287

Authors: Pascal Reisewitz, David Hinds, Sara Dosenovic, Yonghao Ma, Ashok Jha, Abigail Hunt, Barbara K. Burton, Nathalie Guffon

Institutions: BioMarin (United States), Northwestern University, Hospices Civils de Lyon

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4319459709

FWCI:

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