Intracellular stability and efficacy of β-galactosidase fusions as a GM1 gangliosidosis ERT are significantly influenced by mouse versus human multi-enzyme complex interactions
Year: 2023
Type: article
Study design: Case Report
Authors: Tianhong Yang, Walter L. Acosta, Jorge Ayala, Shivakumar Pattada, Kassandra Riley, Rachel Hampton, David Radin, Carole L. Cramer
Language: English
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4319460076
