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A pilot study evaluating the use of sirolimus in children and young adults with desmoid‐type fibromatosis

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Year: 2023
Type: article
Study design: Clinical Trial
Source: Pediatric Blood & Cancer
DOI: 10.1002/pbc.30466
Authors: Aaron R. Weiss, Sarah Dry, Clara Maygar, Anya Cutler, Christine W. Lary, Carmen Khoo, Jillian E. Fergione, Melanie M. Hounchell, Kathleen Glick, Meghen Browning, Sun Ha Choo, Douglas S. Hawkins, Joanne Lagmay, Michelle Manalang, Stephen X. Skapek, Brenda Weigel, Stephanie Verwys, Noah Federman
Institutions: Maine Medical Center, Maine Medical Center, University of California, Los Angeles, MaineHealth, Northeastern University, Children's Hospital of Wisconsin, Rady Children's Hospital-San Diego, Seattle Children's Hospital, University of Washington, University of Florida Health, University of Florida, University of Florida Health Science Center, The University of Texas Southwestern Medical Center, University of Minnesota, Masonic Cancer Center
Language: English

Topic: Soft tissue tumor case studies
Subfield: Rheumatology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: Desmoid Tumor Research Foundation, Pfizer
OpenAlex ID: W4379599347
FWCI: 1.726
Cites: 14
Cited by: 10
Related to: 10
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