Work

AAV-based in vivo gene therapy for neurological disorders

Year: 2023

Type: review

Source: Nature Reviews Drug Discovery

DOI: 10.1038/s41573-023-00766-7

Authors: Qinglan Ling, Jessica A. Herstine, Allison Bradbury, Steven J. Gray

Institutions: The University of Texas Southwestern Medical Center, Nationwide Children's Hospital, The Ohio State University

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

Funder: Eunice Kennedy Shriver National Institute of Child Health and Human Development

Award: First murine animal model and adeno-associated virus (AAV)-based gene therapy for MTATP6 mitochondrial diseases

OpenAlex ID: W4386360124

FWCI: 7.787

Cites: 190

Cited by: 203

Related to: 10