Work

P28 The antisense oligonucleotide BMN 351 durably ameliorates dystrophic phenotypes in a mouse model of exon 51–skip-amenable Duchenne muscular dystrophy

Year: 2023

Type: conference-abstract

Source: Neuromuscular Disorders

DOI: 10.1016/j.nmd.2023.07.155

Authors: D. Porco, D. Neil, B. Crawford, C. O'Neill, Y. Qi, T. Oppeneer, K. Larimore, S. Gupta, F. Beretta

Institution: BioMarin (United States)

Language: English

Topic: Muscle Physiology and Disorders

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4387307213

Cites:

Cited by: 5

Related to: 10