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P210 Interim results from the RESPOND study evaluating nusinersen in children with spinal muscular atrophy previously treated with onasemnogene abeparvovec

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Year: 2023
Type: conference-abstract
Source: Neuromuscular Disorders
DOI: 10.1016/j.nmd.2023.07.092
Authors: J. Parsons, N. Kuntz, J. Brandsema, C. Proud, R. Finkel, K. Swoboda, R. Masson, R. Foster, Y. Liu, C. Makepeace, S. Singhi, A. Paradis, Z. Berger, S. Rane, K. Somera-Molina
Institutions: Children's Hospital Colorado, Lurie Children's Hospital, Children's Hospital of Philadelphia, Children's Hospital of The King's Daughters, St. Jude Children's Research Hospital, Massachusetts General Hospital, Fondazione IRCCS Istituto Neurologico Carlo Besta, Biogen (United Kingdom), Biogen (United States)
Language: English

Topic: Neurogenetic and Muscular Disorders Research
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4387310229
Cites:
Cited by: 2
Related to: 10
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