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P363 The AMETHIST phase 3 trial of venglustat in patients with GM2 gangliosidoses and related diseases: baseline characteristics

Year: 2023

Type: conference-abstract

Source: Neuromuscular Disorders

DOI: 10.1016/j.nmd.2023.07.470

Authors: R. Zheng, C. Tifft, P. Minini, I. Batsu

Institutions: National Institutes of Health, Sanofi (France)

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology (medical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4387310728

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