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276 Delivery of CFTR mRNA using polymeric nanoparticles in a cystic fibrosis mouse model

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Year: 2023
Type: article
Source: Journal of Cystic Fibrosis
DOI: 10.1016/s1569-1993(23)01204-3
Authors: A. Garrison, A. Suberi, J. Browne, D. Eaton, L. Akhtar, T. Kockar Kizilirmak, E. Bruscia, A. Piotrowski-Daspit, W. Saltzman, M Egan
Institution: Yale University
Language: English

Topic: RNA Interference and Gene Delivery
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: National Institutes of Health, National Heart, Lung, and Blood Institute
Awards: G4262198647, In vivo delivery of engineered tRNAs for suppression of nonsense mutations
OpenAlex ID: W4387746815
FWCI:
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Cited by:
Related to: 10
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